Enabling treatments for rare diseases
OpenTreatments software platform streamlines therapy development for any monogenic rare disease regardless of rarity and geography
Our Mission
Our Goal, Vision and Commitment
Our Platform
A software to accelerate treatments
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Empowered to take action
When it comes to finding treatments for rare diseases patients lead the charge. Without a formal background, they must learn biology, speak like a scientist, raise millions of dollars, conduct research, and move mountains to find a treatment. They are often asked to make life-altering decisions without much background, or support. OpenTreatments Foundation empowers these patient organizations by giving them the software tools to make the right decisions at the right time, with a system of support.
Simplify the maze
Patient organizations are left to navigate the complex treatment development maze. Each patient group creates their own research program without a deep understanding of the risks, benefits, and pitfalls of their decisions. OpenTreatments platform simplifies the maze by bringing in real-world experience along every step leading to faster treatments.
Our Collaborators
OpenTreatments Platform
A software platform to give patients the tools and technology to build treatments for any monogenic rare disease
Try OpenTreatments Platform
We are currently piloting OpenTreatments platform with with 4 patient led organizations
Join the waitlist to get priority access when we open more broadly.
"OpenTreatments will enable IDefine to accelerate our mission by distilling down the necessary steps in the development of a gene therapy program into a concise and approachable plan"
- Geoff Rhyne
Co-Founder and CEO of IDefine, a patient-led organization tackling Kleefstra Syndrome caused by mutations in EHMT1 gene.